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IM-MV 18-003_004
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UMCG
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Study of Adeno-Associated Virus (AAV) Serotype 8 (AAV8)-Mediated Gene Transfer of Glucose-6-Phosphatase (G6Pase) in subjects with Glycogen Storage Disease Type la (GSDIa)
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21-12-2021
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Vergunning verleend
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IM-MV 19-024_003
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Stichting Radboud Universiteit
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EXPLORE: A Phase II, masked multicentre, randomised study to evaluate the safety and efficacy of two doses of GT005 administered as a single subretinal injection in subjects with geographic atrophy secondary to age-related macular degeneration
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30-12-2021
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Vergunning verleend
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IM-MV 21-004_000
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Stichting Radboud Universiteit
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Open-Label, Single Ascending Dose Study to Evaluate the Safety, Tolerability, and Efficacy of EDIT-101 in Adult and Pediatric Participants with Leber Congenital Amaurosis Type 10 (LCA10), with Centrosomal Protein 290 (CEP290)-Related Retinal Degeneration Caused by a Compound Heterozygous or Homozygous Mutation Involving c.2991+1655A>G in Intron 26 (IVS26) of the CEP290 Gene (“LCA10-IVS26”)
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16-12-2021
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Vergunning verleend
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IM-MV 21-024_000
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Het Nederlands Kanker Instituut
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Application of nuclease-mediated TCR gene editing of an autologous T cell product targeting a limited number of tumor-specific neoantigens for the treatment of advanced solid tumors
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10-12-2021
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Vergunning verleend
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